Rare diseases Xagena
Researchers have found that genetic alterations originally identified in people suffering from a rare disease may also be an important risk factor for the second most common form of dementia among the ...
The FDA ( Food and Drug Administration ) has approved Cerdelga ( Eliglustat ) capsules, the only first-line oral therapy for certain adult Gaucher disease type 1 patients. A small number of adult pa ...
The FDA ( Food and Drug Administration ) has approved Cerdelga ( Eliglustat ) capsules, the only first-line oral therapy for certain adult Gaucher disease type 1 patients. A small number of adult pati ...
The results from the ENCORE study exploring Cerdelga ( Eliglustat ) as a maintenance therapy suitable for adult patients who had reached pre-specific treatment goals on enzyme replacement therapy ( ER ...
